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2020•NeurologyRequires access

Nusinersen Initiation in Adults with Spinal Muscular Atrophy (4906)

Maha Daimee, Nayar Shakti

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Abstract

Case series of adults that initiated nusinersen intrathecal infusions for spinal muscular atrophy (SMA types 2 or 3) in adulthood. We sought to report measures of functional capacity at baseline and during therapy, through serial evaluations and patient’s subjective experience. Our center’s experience is unique as it serves adult SMA patients who live in the Washington, DC tri-state area.

About this research paper

What this paper is about

Case series of adults that initiated nusinersen intrathecal infusions for spinal muscular atrophy (SMA types 2 or 3) in adulthood. We sought to report measures of functional capacity at baseline and during therapy, through serial evaluations and patient’s subjective experience. Our center’s experience is unique as it serves adult SMA patients who live in the Washington, DC tri-state area.

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Available abstract

Case series of adults that initiated nusinersen intrathecal infusions for spinal muscular atrophy (SMA types 2 or 3) in adulthood. We sought to report measures of functional capacity at baseline and during therapy, through serial evaluations and patient’s subjective experience. Our center’s experience is unique as it serves adult SMA patients who live in the Washington, DC tri-state area.

Key concepts: Spinal muscular atrophy, Progressive muscular atrophy, Medicine, Atrophy, Physical medicine and rehabilitation, Pathology, Amyotrophic lateral sclerosis, Disease

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