2023•Neuromuscular DisordersRequires access
P62 SIMPATHIC: accelerating drug repurposing for rare neurological, neurometabolic and neuromuscular disorders by exploiting SIMilarities in clinical and molecular PATHology
P. 't Hoen, L. Benkemoun, Alessandro Prigione, Ibrahim Boussaad, Martin de Kort, A. Geille, Hanns Lochmüller, Nicol Cornelia Voermans, Baziel G.M. van Engelen, Clara van Karnebeek
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Abstract
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