2022•Genetics in MedicineRequires access
OP005: AT-007 significantly reduces toxic galactitol in ACTION-galactosemia kids - the 1st therapeutic interventional clinical trial in children with classic galactosemia
Evan Bailey, Stella Wang, Laura Saltonstall, Riccardo Perfetti, Shoshana Shendelman
Open publisher page 3 citations
Abstract
This record does not include an abstract. Use the full-text link above if available.