HELIOS-A: RESULTS FROM THE PHASE 3 STUDY OF VUTRISIRAN IN PATIENTS WITH HEREDITARY TRANSTHYRETIN-MEDIATED AMYLOIDOSIS WITH POLYNEUROPATHY
Alejandra González‐Duarte, David Adams, Ivailo Tournev, Mark Taylor, Teresa Coelho, Violaine Planté‐Bordeneuve, John L. Berk, Julian D. Gillmore, Soon-Chai Low, Yoshiki Sekijima, Laura Obici, Chongshu Chen, Prajakta Badri, Seth Arum, John Vest, Michael Polydefkis
Abstract
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