Towards regulatory endorsement of drug development tools to promote the application of model-informed drug development in Duchenne muscular dystrophy
Daniela J. Conrado, Jane Larkindale, Alexander K. Berg, Micki Hill, Jackson K. Burton, Keith R. Abrams, Richard Ted Abresch, Abby Bronson, Douglass S. Chapman, Michael J. Crowther, Tina Duong, Heather Gordish‐Dressman, Lutz O. Harnisch, Erik Henricson, Sarah Kim, Craig M. McDonald, Stephan Schmidt, Camille Vong, Xiaoxing Wang, Brenda L. Y. Wong, Florence H. Yong, Klaus Romero
Abstract