Outcome measures for Duchenne muscular dystrophy from ambulant to non-ambulant: Implications for clinical trials
Joana Domingos, Michelle Eagle, Amélie Moraux, Jordan W. Butler, V. Decostre, Deborah A. Ridout, A. Mayhew, Victoria L. Selby, Michela Guglieri, Menno van der Holst, Merel Jansen, Jan J.G.M. Verschuuren, Imelda J. M. de Groot, Erik Harmen Niks, Laurent Servais, Jean‐Yves Hogrel, Volker W. Straub, Thomas Voit, V. Ricotti, Francesco Muntoni
Abstract