Engraftment of gene–modified umbilical cord blood cells in neonates with adenosine deaminase deficiency
Donald B. Kohn, Kenneth I. Weinberg, Jan A. Nolta, Linda N. Heiss, Carl Lenarsky, Gay M. Crooks, Mary E. Hanley, Geralyn Annett, Judith Brooks, Anthony El-Khoureiy, Kim Lawrence, Susie Wells, Robert C. Moen, John F. Bastian, Debora Williams‐Herman, Melissa E. Elder, Diane W. Wara, Thomas J. Bowen, Michael S. Hershfield, Craig A. Mullen, R. Michael Blaese, Robertson Parkman
Abstract