Strict cysteamine dose regimen is required to prevent nocturnal cystine accumulation in cystinosis
Elena N. Levtchenko, Carin M. van Dael, Adriana de Graaf-Hess, Martijn J. G. Wilmer, Lambertus P. van den Heuvel, Leo A.H. Monnens, Henk J. Blom
Abstract