Gene therapy for immunodeficiency diseases
Alain Fischer, Salima Hacein‐Bey‐Abina, Marina Cavazzana
Abstract
Alain Fischer, Salima Hacein‐Bey‐Abina, Marina Cavazzana
Abstract
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Key concepts: Genetic enhancement, Severe combined immunodeficiency, Lentivirus, Immunodeficiency, Primary immunodeficiency, Viral vector, Haematopoiesis, Hematopoietic stem cell transplantation