Mice lacking both subunits of lysosomal β–hexosaminidase display gangliosidosis and mucopolysaccharidosis
Kazunori Sango, Michael P. McDonald, Jacqueline N. Crawley, Michelle L. Mack, Cynthia J. Tifft, Elisa Skop, Christopher M. Starr, Alexander Hoffmann, Konrad Sandhoff, Kinuko Suzuki, Richard L. Proia
Abstract