Life-threatening hypophosphatasia (HPP): Results of up to two years bone-targeted Enzyme Replacement Therapy (ERT) in infants and young children
Nick J. Bishop, Cheryl R. Greenberg, Stan Craig, Mairead McGinn, Jill H. Simmons, William E. Russell, Melissa Bauer, John William Taylor, N. Salman, Mukhri Hamdan, Michael B. Bober, Jean N. Moore, Richard E. Lutz, Deborah Wenkert, William Howard McAlister, Alison M. Skrinar, Hal Landy, Michael P. Whyte
Abstract